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dc.creatorGarcía Fernández, José Manueles
dc.creatorOrtiz Mellet, Carmenes
dc.date.accessioned2022-12-14T16:03:11Z
dc.date.available2022-12-14T16:03:11Z
dc.date.issued2019
dc.identifier.citationGarcía Fernández, J.M. y Ortiz Mellet, C. (2019). Novel Therapies for Orphan Diseases. ACS Medicinal Chemistry Letters, 10 (7), 1020-1023. https://doi.org/10.1021/acsmedchemlett.9b00242.
dc.identifier.issn1948-5875es
dc.identifier.urihttps://hdl.handle.net/11441/140467
dc.description.abstract"Orphan" does not mean infrequent: over 7000 rare diseases affect millions of individuals. The US Orphan Drug Act and analogous regulations have succeeded at accelerating the development of novel therapies, but high prices threaten sustainability. Lysosomal storage disorders serve here to illustrate the light and shadows of this burgeoning field.es
dc.formatapplication/pdfes
dc.format.extent8 p.es
dc.language.isoenges
dc.publisherAmerican Chemical Societyes
dc.relation.ispartofACS Medicinal Chemistry Letters, 10 (7), 1020-1023.
dc.rightsAttribution-NonCommercial-NoDerivatives 4.0 Internacional*
dc.rights.urihttp://creativecommons.org/licenses/by-nc-nd/4.0/*
dc.titleNovel Therapies for Orphan Diseaseses
dc.typeinfo:eu-repo/semantics/articlees
dcterms.identifierhttps://ror.org/03yxnpp24
dc.type.versioninfo:eu-repo/semantics/acceptedVersiones
dc.rights.accessRightsinfo:eu-repo/semantics/openAccesses
dc.contributor.affiliationUniversidad de Sevilla. Departamento de Química orgánicaes
dc.relation.publisherversionhttps://dx.doi.org/10.1021/acsmedchemlett.9b00242es
dc.identifier.doi10.1021/acsmedchemlett.9b00242es
dc.journaltitleACS Medicinal Chemistry Letterses
dc.publication.volumen10es
dc.publication.issue7es
dc.publication.initialPage1020es
dc.publication.endPage1023es

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