- idUS
- Listar por autor
Listar por autor "Videla, Sebastián"
Mostrando ítems 1-1 de 1
-
Artículo
Efficacy and safety clinical trial with efavirenz in patients diagnosed with adult Niemann-pick type C with cognitive impairment
Gascón Bayarri, Jordi; Simon, Petru Cristian; Llop, Roser; Carnaval, Thiago; Ledesma, María Dolores; Rico, Imma; Mir Rivera, Pablo; Videla, Sebastián (Lippincott, Williams & Wilkins, 2022-12-02)Background: Niemann-Pick disease Type C (NPC) is a genetic, incurable, neurodegenerative disorder. This orphan disease ...